Will Forte, who played MacGruber on Saturday Night Live, and his brother-in-law Doug Modling, who has Huntington's Disease, ...
FDA Commissioner Marty Makary defended the agency’s recent rejections of rare disease drugs and one of his deputies, Vinay ...
Rare diseases are not actually that rare. Collectively they affect 500 million people around the world. Some, such as Huntington’s disease and sickle cell disease, affect many thousands, others only ...
At the American Athletic Conference championships in Greensboro, N.C., several Herd swimmers took home medals and set new program records.
A man murdered his girlfriend at a hotel while the pair were on vacation and smuggled the body out of the building by hiding it on a luggage cart.
The rare genetic condition affects muscles and other vital systems of the body, including the heart and lungs, and is characterised by progressive muscle weakness and wasting.
Interview with award-winning correspondent Liz Cookman on war reporting after leaving school at 15 and a recent ADHD ...
A panel of physicians, biotech leaders and patient advocates took aim at the FDA during a Senate hearing Thursday on how the ...
The Marshall University Psychology Clinic is celebrating National Anxiety Screening Day by offering free anxiety screenings on Wednesday, March 4. The university ...
Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today reported financial results for the fourth quarter and full-year 2025.
Margaret Tobin accepted a three-week babysitting gig in 1989 for a newborn named Audrey that turned into a life-long relationship. The two women talk about their life together.
After decades of service, caregiving, and volunteer work, Mary Flatley is celebrating a long-awaited publishing milestone.